您好,欢迎来到维库仪器仪表网 免费注册 登录 忘记密码
bluebird bio
美国bluebirdbiowww.bluebirdbio.com单基因突变基因疗法bluebirdbio isdevelopinginnovativegenetherapiesforseveregeneticdisorders. Attheheartofbluebirdbio’sproductcreationeffortsisitsbroadlyapplicablegenetherap yplatformforthedevelopmentofnoveltreatmentsfordiseaseswithfewornoclinicaloptions. Thecompany’snovelapproachusesstemcellsharvestedfromthepatient’sbonemarrowintowhichahealthyversionofthediseasecausinggeneisinserted. Afterbeinggrowninculture,thosecellsaregivenbacktothepatient. bluebirdbio’sapproach representsatrueparadigmshiftinthetreatmentofseveregeneticdiseasesbyeliminatingthepotentialcomplicationsassociatedwithdonorcelltransplantationandpotentiallypresentingaone-timetransformativetherapy.bluebirdbiohastwolaterstageclinicalproductsindevelopmentforchildhoodcerebraladrenoleukodystrophy(CCALD)
暂无相关代理商