Sarepta Therapeutics(美国)

Sarepta Therapeutics

美国SareptaTherapeutics www.sareptatherapeutics.com公司是一家生物制药公司，研究和开发以抗转录疗法和癌症免疫疗法技术为基础的治疗性产品.该公司成立于1980年，总部在美国华盛顿， isfocusedondevelopingfirst-in-classRNA-basedtherapeuticstoimproveandsavethelivesofpeop leaffectedbyseriousandlife-threateningrareandinfectiousdiseases.TheCompany'sdiversepipelineincludesitsleadprogrameteplirsen,forDuchennemusculardystrophy,aswellaspotentialtreatmentsforsomeoftheworld'smostlethalinfectiousdiseases.Sareptaaimstobuildaleading,independentbiotechcompanydedicatedtotranslatingitsRNA-basedscienceintotransformationaltherapeuticsforpatientswhofacesignificantunmetmedicalneeds.