MyoKardia(美国)
MyoKardia
MyoKardiawww.myokardia.comMyoKardiaisdedicatedtorevolutionizingthetreatmentofcardiovasculardisease.Thecompany'sfirstprogramsincludehypertrophicanddilatedcardiomyopathy(HCMandDCM),whichtogetherafflicta
pproximately1millionpeopleintheUnitedStates,andforwhichnonoveltherapeuticshavebeenbroughttomarketinoveradecade.TargetingDiseaseattheSourceMyoKardia'sproprietarydrugdiscoveryplatformbringstogetheradvancesfromthefieldsofcardiovasculargenomicsandheartmusclebiologytoenableitsscientiststotargetcertainheartdisease'atitssource.'Abnormalitiesinthebasicunitofheartmuscle,calledthesarcomeres,havebeenidentifiedasthedrivingcauseforavarietyofheartdisease,andthemostcommoncauseofhypertrophicanddilatedcardiomyopathy.Mutationsintheproteinsofthesarcomerecausediseasebyrenderingthemuscleeither'hyper'or'hypo'contractile.Develo